Fri, 2 October, 10:30-12:00
Chairs:
- Blood biomarkers for longitudinal monitoring in adult 5q spinal muscular atrophy (SMA) (C. Stapf, Halle)
- Metabolic alterations in Spinal Muscular Atrophy (C. Herrmann, Ulm)
- Long-term trajectories of multimdimensional fatigue in adults with 5q-spinal muscular atrophy receiving disease-modifying therapy (Bogdan Bjelica, Hannover)
- Biomarker potential of established and exploratory serum muscle parameters in adult patients with SMA before and during treatment with nusinersen and risdiplam (H. Lapp, Dresden)
- Challenges and opportunities of current and future SMA therapies (T. Hagenacker, Essen)